Leber hereditary optic neuropathy (LHON) is a genetic mitochondrial disorder that damages retinal ganglion cells, resulting in rapid vision loss. Idebenone is expected to restore mitochondrial ...
Program underscores Stealth's commitment to patient access and partnership with the Barth syndrome community NEEDHAM, Mass., ...
New findings show Telomir-1 shuts down cellular energy pathways and mitochondrial function in aggressive breast cancer cells, ...
The FDA approves Forzinity (elamipretide HCl) to improve muscle strength in adult and pediatric patients with Barth syndrome weighing at least 30kg.
Northwestern University professor Hande Ozdinler is hoping to change how ALS is treated, saying the disease is too complex ...
Findings show that Telomir-1 restores the body's natural tumor suppressor defenses by reversing abnormal DNA methylation of MASPIN and RASSF1A - genes that help block invasion, limit metastasis, and i ...
Precision BioSciences, Inc. (Nasdaq: DTIL), a clinical stage gene editing company utilizing its novel proprietary ARCUS ® platform to develop in vivo gene editing therapies for diseases with ... e.g.
A key switch for cellular energy balance has been discovered in cells: it could potentially become the target of new ...
A key switch for cellular energy balance has been discovered in cells, and it could potentially become the target of new ...
First-of-its-kind therapy developed by Johns Hopkins researchers cleared for treatment of Barth syndrome, a condition that ...
Research led by the Max Planck Institute for Biology of Aging in Cologne reports that misincorporation of ribonucleotides ...