People with irritable bowel syndrome are often only given treatments like cognitive behavioural therapy after others have ...

Americans who are suffering debilitating symptoms deserve answers—and treatment.

The U.S. Food and Drug Administration has granted accelerated approval to Forzinity (elamipretide) injection as the first ...

The FDA has granted accelerated approval for the elamipretide injection, the first treatment for Barth syndrome in patients weighing at least 30 ...

Victor Sung, M.D., director of the Division of Movement Disorders in the University of Alabama at Birmingham Department of ...

The FDA approves Forzinity (elamipretide HCl) to improve muscle strength in adult and pediatric patients with Barth syndrome weighing at least 30kg.

MIDDLETON, Mass., Sept. 22, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...

Noonan syndrome with multiple lentigines (NSML) is a rare genetic disorder that causes short stature, distinctive facial features, and clusters of dark skin spots called lentigines. But its most ...

Ed Silverman, a senior writer and Pharmalot columnist at STAT, has been covering the pharmaceutical industry for nearly three decades. He is also the author of the morning Pharmalittle newsletter and ...

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The Los Angeles County Board of Supervisors unanimously approved rent relief funds for those impacted by the January wildfires and for residents affected by recent federal immigrant enforcement ...

LOS ANGELES (CNS) -- The county Board of Supervisors on Tuesday unanimously approved the creation of a roughly $30 million emergency rent-relief program to assist people still dealing with income or ...