Forzinity traveled an unusual route to approval and, along the way, became a test case for the agency’s willingness to be flexible with medicines for ultra-rare conditions. Formerly known as ...
FITBOOK magazine on MSN
Rett Syndrome: When Parents Suddenly Don’t Recognize Their Child
After an uneventful first year of life, children suddenly lose skills they had already acquired. What is Rett Syndrome? Rett syndrome (RTT) is a neurological developmental disorder caused by ...
Barth syndrome primarily affects boys due to its X chromosome mutation pathogenesis. Credit: Anusorn Nakdee via Shutterstock.com. After a rocky regulatory pathway filled with delays and a previous ...
A little known condition can cause terrifying and incurable skin growths, with many having no choice but to face amputation. The rare condition, known as epidermodysplasia verruciformis, is only known ...
A decade-long journey has come to an end for Stealth BioTherapeutics and the Barth syndrome community with the first-ever treatment for this uncommon mitochondrial disease. CEO Reenie McCarthy called ...
Growing up as the oldest sibling, author Y.L. Wolfe often felt the lines between her role and her mother’s role were blurred. “By the time my youngest brother was born when I was almost 11, I was ...
This is an edition of The Wonder Reader, a newsletter in which our editors recommend a set of stories to spark your curiosity and fill you with delight. Sign up here to get it every Saturday morning.
A 13-year-old boy with Tourette's syndrome killed himself over brutal bullying after he accidentally shared a nude video with his classmates, according to his family. Gabriel Palacios died by suicide ...
Texas has executed four people so far this year – a low number, considering the state often executed that many per month during the 1990s and 2000s. No executions were scheduled at all this summer and ...
MORGANTOWN, W.Va. (WBOY) — While Alpha-gal Syndrome may not be exactly new to West Virginia, the Monongalia County Health Department has confirmed the county’s first official case since the condition ...
Copyright 2025 The Associated Press. All Rights Reserved. Copyright 2025 The Associated Press. All Rights Reserved. (AP Illustration / Peter Hamlin) NEW YORK (AP ...
Shale wells decline fast, forcing constant drilling—the “Red Queen” effect—with many losing 70–90% of output in three years. The IEA says global fields are depleting faster than thought, so most ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback