Forzinity traveled an unusual route to approval and, along the way, became a test case for the agency’s willingness to be flexible with medicines for ultra-rare conditions. Formerly known as ...
Barth syndrome primarily affects boys due to its X chromosome mutation pathogenesis. Credit: Anusorn Nakdee via Shutterstock.com. After a rocky regulatory pathway filled with delays and a previous ...
A little known condition can cause terrifying and incurable skin growths, with many having no choice but to face amputation. The rare condition, known as epidermodysplasia verruciformis, is only known ...
A decade-long journey has come to an end for Stealth BioTherapeutics and the Barth syndrome community with the first-ever treatment for this uncommon mitochondrial disease. CEO Reenie McCarthy called ...
Growing up as the oldest sibling, author Y.L. Wolfe often felt the lines between her role and her mother’s role were blurred. “By the time my youngest brother was born when I was almost 11, I was ...
During a House Judiciary Committee hearing several days ago, Congresswoman Becca Balint (D-VT) called out FBI Director Kash Patel on his and the Trump Administration's double standard, as their ...
This is an edition of The Wonder Reader, a newsletter in which our editors recommend a set of stories to spark your curiosity and fill you with delight. Sign up here to get it every Saturday morning.
A 13-year-old boy with Tourette's syndrome killed himself over brutal bullying after he accidentally shared a nude video with his classmates, according to his family. Gabriel Palacios died by suicide ...
Texas has executed four people so far this year – a low number, considering the state often executed that many per month during the 1990s and 2000s. No executions were scheduled at all this summer and ...
MORGANTOWN, W.Va. (WBOY) — While Alpha-gal Syndrome may not be exactly new to West Virginia, the Monongalia County Health Department has confirmed the county’s first official case since the condition ...
Rep. Becca Balint, whose grandfather was murdered in the Holocaust, also used the term for the first time Wednesday. Bernie Sanders has become the first U.S. senator to label Israel’s conduct in Gaza ...
Copyright 2025 The Associated Press. All Rights Reserved. Copyright 2025 The Associated Press. All Rights Reserved. (AP Illustration / Peter Hamlin) NEW YORK (AP ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback